Difference between revisions of "Verbrinacogene setparvovec (FLT-180a)"

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==Preliminary data==
 
==Preliminary data==
 
===[[Inherited coagulopathy|Hemophilia B]]===
 
===[[Inherited coagulopathy|Hemophilia B]]===
#'''B-AMAZE:''' Chowdary P, Shapiro S, Makris M, Evans G, Boyce S, Talks K, Dolan G, Reiss U, Phillips M, Riddell A, Peralta MR, Quaye M, Patch DW, Tuddenham E, Dane A, Watissée M, Long A, Nathwani A. Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B. N Engl J Med. 2022 Jul 21;387(3):237-247. [https://doi.org/10.1056/nejmoa2119913 link to original article] [https://pubmed.ncbi.nlm.nih.gov/35857660/ PubMed] NCT03369444; NCT03641703
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#'''B-AMAZE:''' Chowdary P, Shapiro S, Makris M, Evans G, Boyce S, Talks K, Dolan G, Reiss U, Phillips M, Riddell A, Peralta MR, Quaye M, Patch DW, Tuddenham E, Dane A, Watissée M, Long A, Nathwani A. Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B. N Engl J Med. 2022 Jul 21;387(3):237-247. [https://doi.org/10.1056/nejmoa2119913 link to original article] [https://pubmed.ncbi.nlm.nih.gov/35857660/ PubMed] [https://clinicaltrials.gov/study/NCT03369444 NCT03369444]; [https://clinicaltrials.gov/study/NCT03641703 NCT03641703]
  
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==Also known as==
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*'''Code name:''' FLT-180a
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[[Category:Drugs]]
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[[Category:Intravenous medications]]
 
[[Category:Inherited coagulopathy medications (investigational)]]
 
[[Category:Inherited coagulopathy medications (investigational)]]
 
[[Category:Investigational drugs]]
 
[[Category:Investigational drugs]]
 
[[Category:Stub]]
 
[[Category:Stub]]

Latest revision as of 02:20, 26 July 2023

Gene therapy

Preliminary data

Hemophilia B

  1. B-AMAZE: Chowdary P, Shapiro S, Makris M, Evans G, Boyce S, Talks K, Dolan G, Reiss U, Phillips M, Riddell A, Peralta MR, Quaye M, Patch DW, Tuddenham E, Dane A, Watissée M, Long A, Nathwani A. Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B. N Engl J Med. 2022 Jul 21;387(3):237-247. link to original article PubMed NCT03369444; NCT03641703

Also known as

  • Code name: FLT-180a