Betibeglogene autotemcel (Zynteglo)

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Mechanism of action

Gene therapy using autologous hematopoietic stem and progenitor cells transduced with BB305 lentiviral vector.

History of changes in FDA indication

  • 2022-08-17: Approved for treatment of adult and pediatric patients with ß-thalassemia who require regular red blood cell (RBC) transfusions. (Based on HGB-207 and HGB-212)

Also known as

  • Generic name: beti-cel
  • Brand name: Zynteglo